| # | Drug |
|---|---|
| 1 | amifampridine |
| 2 | arimoclomol |
| 3 | deutetrabenazine |
| 4 | dextromethorphan |
| 5 | edaravone |
| 6 | eplontersen |
| 7 | fampridine |
| 8 | inotersen |
| 9 | laquinimod |
| 10 | levacetylleucine |
| 11 | omaveloxolone |
| 12 | patisiran |
| 13 | phenylbutanoic acid |
| 14 | pitolisant |
| 15 | riluzole |
| 16 | sodium oxybate |
| 17 | tafamidis |
| 18 | taurursodiol |
| 19 | tetrabenazine |
| 20 | tirilazad |
| 21 | tofersen |
| 22 | trofinetide |
| 23 | valbenazine |
| 24 | vutrisiran |