Stem definition | Drug id | CAS RN |
---|---|---|
gene therapy products | 5172 | 929881-05-0 |
Molecule | Description |
---|---|
Synonyms:
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gene therapy product, contains the human lipoprotein lipase (LPL) gene variant LPLS447X in a vector comprised of a protein shell derived from adeno-associated virus serotype 1 (AAV1), the Cytomegalovirus (CMV) promoter, a woodchuck hepatitis virus posttranscriptional regulatory element and AAV2 derived inverted terminal repeats
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Date | Agency | Company | Orphan |
---|---|---|---|
Oct. 25, 2012 | EMA | uniQure biopharma B.V. |
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Source | Code | Description |
---|---|---|
ATC | C10AX10 | CARDIOVASCULAR SYSTEM LIPID MODIFYING AGENTS LIPID MODIFYING AGENTS, PLAIN Other lipid modifying agents |
Disease | Relation | SNOMED_ID | DOID |
---|---|---|---|
Familial lipoprotein lipase deficiency | indication | 238086005 |
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ID | Source |
---|---|
20OK4AFR4Y | UNII |
C3653189 | UMLSCUI |
CHEMBL2108304 | ChEMBL_ID |
5816 | PUBCHEM_CID |
DB13521 | DRUGBANK_ID |
8987 | INN_ID |
C000721108 | MESH_SUPPLEMENTAL_RECORD_UI |
016036 | NDDF |
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