Stem definition | Drug id | CAS RN |
---|---|---|
enzymes | 5028 | 1276027-63-4 |
Molecule | Description |
---|---|
Synonyms:
|
a recombinant form of human lysosomal acid lipase (rhLAL)
|
Dose | Unit | Route |
---|---|---|
5 | mg | P |
None
Date | Agency | Company | Orphan |
---|---|---|---|
Aug. 28, 2015 | EMA | ||
Dec. 8, 2015 | FDA | ALEXION PHARM |
None
None
None
None
Source | Code | Description |
---|---|---|
ATC | A16AB14 | ALIMENTARY TRACT AND METABOLISM OTHER ALIMENTARY TRACT AND METABOLISM PRODUCTS OTHER ALIMENTARY TRACT AND METABOLISM PRODUCTS Enzymes |
FDA CS | M0004273 | Sterol Esterase |
FDA EPC | N0000192342 | Hydrolytic Lysosomal Cholesteryl Ester-specific Enzyme |
FDA EPC | N0000192343 | Hydrolytic Lysosomal Triacylglycerol-specific Enzyme |
Disease | Relation | SNOMED_ID | DOID |
---|---|---|---|
Wolman's disease | indication | 82500001 | DOID:14497 |
None
None
None
None
None
None
ID | Source |
---|---|
K4YTU42T8G | UNII |
D10377 | KEGG_DRUG |
4035217 | VANDF |
C4050579 | UMLSCUI |
CHEMBL3039537 | ChEMBL_ID |
DB11563 | DRUGBANK_ID |
9594 | INN_ID |
C000603932 | MESH_SUPPLEMENTAL_RECORD_UI |
1726975 | RXNORM |
237417 | MMSL |
31344 | MMSL |
d08404 | MMSL |
016549 | NDDF |
719375007 | SNOMEDCT_US |
763523006 | SNOMEDCT_US |
71354164 | PUBCHEM_CID |
Product | Category | Ingredients | NDC | Form | Quantity | Route | Marketing | Label |
---|---|---|---|---|---|---|---|---|
KANUMA | HUMAN PRESCRIPTION DRUG LABEL | 1 | 25682-007 | INJECTION, SOLUTION, CONCENTRATE | 2 mg | INTRAVENOUS | BLA | 28 sections |
KANUMA | HUMAN PRESCRIPTION DRUG LABEL | 1 | 25682-007 | INJECTION, SOLUTION, CONCENTRATE | 2 mg | INTRAVENOUS | BLA | 28 sections |
KANUMA | HUMAN PRESCRIPTION DRUG LABEL | 1 | 25682-007 | INJECTION, SOLUTION, CONCENTRATE | 2 mg | INTRAVENOUS | BLA | 28 sections |