| Stem definition | Drug id | CAS RN |
|---|---|---|
| 5707 | 2098615-91-7 |
| Molecule | Description |
|---|---|
|
Synonyms:
|
Eladocagene exuparvovec is a gene therapy medicinal product that expresses the human aromatic L-amino acid decarboxylase enzyme (hAADC). It is a non-replicating recombinant adeno-associated virus serotype 2 (AAV2) based vector containing the cDNA of the human dopa decarboxylase (DDC) gene under the control of the cytomegalovirus immediate-early promoter.
|
None
None
| Date | Agency | Company | Orphan |
|---|---|---|---|
| Aug. 17, 2022 | EMA | PTC Therapeutics International Limited |
None
None
None
None
None
| Disease | Relation | SNOMED_ID | DOID |
|---|---|---|---|
| Deficiency of aromatic-L-amino-acid decarboxylase | indication | 124600004 | DOID:0090123 |
None
None
None
None
None
None
| ID | Source |
|---|---|
| CHEMBL4298189 | ChEMBL_ID |
| DB16780 | DRUGBANK_ID |
| C5419302 | UMLSCUI |
| 10885 | INN_ID |
| D12407 | KEGG_DRUG |
| S51J6N56M7 | UNII |
None