sebelipase alfa 🐶 Veterinary Use | Indications/Contra | FAERs-F | FAERs-M | Orange Bk | BioActivity |

Stem definitionDrug idCAS RN
enzymes 5028 1276027-63-4

Description:

MoleculeDescription

Synonyms:

  • sebelipase alfa
  • SBC-102
  • kanuma
  • LIPA
a recombinant form of human lysosomal acid lipase (rhLAL)
  • Molecular weight:
  • Formula:
  • CLOGP:
  • LIPINSKI: None
  • HAC: None
  • HDO: None
  • TPSA:
  • ALOGS:
  • ROTB: None

Drug dosage:

DoseUnitRoute
5 mg P

ADMET properties:

None

Approvals:

DateAgencyCompanyOrphan
Aug. 28, 2015 EMA
Dec. 8, 2015 FDA ALEXION PHARM

FDA Adverse Event Reporting System (Female)

None

FDA Adverse Event Reporting System (Male)

None

FDA Adverse Event Reporting System (Geriatric)

None

FDA Adverse Event Reporting System (Pediatric)

None

Pharmacologic Action:

SourceCodeDescription
ATC A16AB14 ALIMENTARY TRACT AND METABOLISM
OTHER ALIMENTARY TRACT AND METABOLISM PRODUCTS
OTHER ALIMENTARY TRACT AND METABOLISM PRODUCTS
Enzymes
FDA CS M0004273 Sterol Esterase
FDA EPC N0000192342 Hydrolytic Lysosomal Cholesteryl Ester-specific Enzyme
FDA EPC N0000192343 Hydrolytic Lysosomal Triacylglycerol-specific Enzyme

Drug Use | Suggest Off label Use Form| |View source of the data|

DiseaseRelationSNOMED_IDDOID
Wolman's disease indication 82500001 DOID:14497




🐶 Veterinary Drug Use

None

🐶 Veterinary products

None

Acid dissociation constants calculated using MoKa v3.0.0

None

Orange Book patent data (new drug applications)

None

Orange Book exclusivity data (new drug applications)

None

Bioactivity Summary:

None

External reference:

IDSource
K4YTU42T8G UNII
D10377 KEGG_DRUG
4035217 VANDF
C4050579 UMLSCUI
CHEMBL3039537 ChEMBL_ID
DB11563 DRUGBANK_ID
9594 INN_ID
C000603932 MESH_SUPPLEMENTAL_RECORD_UI
1726975 RXNORM
237417 MMSL
31344 MMSL
d08404 MMSL
016549 NDDF
719375007 SNOMEDCT_US
763523006 SNOMEDCT_US
71354164 PUBCHEM_CID

Pharmaceutical products:

ProductCategoryIngredientsNDCFormQuantityRouteMarketingLabel
KANUMA HUMAN PRESCRIPTION DRUG LABEL 1 25682-007 INJECTION, SOLUTION, CONCENTRATE 2 mg INTRAVENOUS BLA 28 sections
KANUMA HUMAN PRESCRIPTION DRUG LABEL 1 25682-007 INJECTION, SOLUTION, CONCENTRATE 2 mg INTRAVENOUS BLA 28 sections
KANUMA HUMAN PRESCRIPTION DRUG LABEL 1 25682-007 INJECTION, SOLUTION, CONCENTRATE 2 mg INTRAVENOUS BLA 28 sections